Videos

Efficacy of nusinersen in a diverse patient population of teens and adults treated for up to 30 months

What real-world evidence shows on nusinersen in a wide severity spectrum of SMA patients in long-term observation (up to 30 months), including first-ever evidence for efficacy in adults with Type 1 SMA.

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“The evolving landscape of SMA, through challenges and solutions” – Katia Patanella

Techniques to support intrathecal drug administration: In this video you hear about the latest publications from teen and adult cohorts supporting the use of nusinersen in SMA patients

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“Eyes on me, please!” – Ultrasound for IT injection – Bruno Zanfini

Techniques to support intrathecal drug administration: In this video you get acquainted with the growing evidence of ultrasound guided successful lumbar approaches.

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“Experience with CT guided drug administration and 3D spine modelling” – Marek Mechl

Techniques to support intrathecal drug administration: In this video you learn how the use of fluoroscopy can support intrathecal drug administration.

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“Fluoroscopy-guided intrathecal therapy with nusinersen – tips and tricks” – Jaime Pamplona

Techniques to support intrathecal drug administration: In this video you will familiarize yourself with computed tomography guided lumbar punctures and the use of 3D spine modelling.

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Informationsfilm om hur Spinraza (nusinersen) administreras

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Presentation Habilitation and rehabilitation in spinal muscular atrophy

This presentation was hosted by Anna-Karin Kroksmark during 2020's Listen & Learn meeting. It was a break-out session intended for physiotherapists on habilitation and rehabilitation in SMA.

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Discover the latest Real-World Evidence-SMA

A critical review and meta-analysis for more than 2600 SMA patients worldwide. To what extent can a treatment change the natural history outside of the clinical trial profile?

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The importance of RWE in SMA (Rare diseases) and the importance of registries

With the growing body of evidence and an evolving treatment landscape, the classification of subtypes needs a revision and Real-World Evidence becomes more and more important.

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NURTURE-study: presymptomatic infants treated with nusinersen

This short PubExplainer gives you an overview of the results of the March 29, 2019 interim analysis of the NURTURE-study in presymptomatic infants treated with nusinersen by De Vivo et al.

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Results from a German real world cohort study in adult SMA-patients

This PubExplainer, on a publication by Hagenacker et al., provides an overview of one of the largest and most diverse real-world studies in adult SMA-patients. The patients were followed at 10 centers in Germany.

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Real-world data on adult SMA-patients from 18 Italian centers

This PubExplainer, by Maggi et al., provides an overview of one of the largest real-world studies in adult SMA-patients published so far. The patients were followed at 18 centers in Italy.

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Independent meta-analysis of treatment effect with nusinersen

In just a few minutes, this PubExplainer gives you an overview of the results of the independent meta-analysis performed by Coratti et al., on real world treatment effect with nusinersen.

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Fatigable or not? That is the question in SMA

Dr. Bartels explains how to distinguish between perceived fatigue and fatigability and how the endurance shuttle tests can be used to assess fatigability across the SMA spectrum.

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ATEND – an outcome measure developed for adult ”non-sitters” with SMA

Dr. Duong explains why a novel outcome measure is needed for adult non-sitters, how it was developed using a human-centered approach and her experience of using the ATEND both in clinic and remotely.

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Outcome measures in adult SMA patients – a Canadian toolkit

Dr. Rodrigue reviews a Canadian outcome measure toolkit för adults with SMA. He discusses the needs unmet by the existing assessment scales and how digital assessments can be an important complement.

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CHOP-INTEND video instructions

Contains instructions on how to perform CHOP-INTEND and how to complete the test paper

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HFMSE video instructions

Contains instructions on how to perform HFMSE and how to complete the test paper

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RULM video instructions

Contains instructions on how to perform RULM and how to complete the test paper

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Zac Video

This video was developed by Biogen together with other stakeholders and tells the story of Zac, an (imaginary) SMA patient. This video can be used to explain SMA to younger patients.

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Biogen-222858 maj 2024
Senast uppdaterad: 2024-05-27